Asset Details

MbrlCatalogueTitleDetail

Do you wish to reserve the book?

Elexacaftor–Tezacaftor–Ivacaftor for Cystic Fibrosis with a Single Phe508del Allele

by Lands, Larry C , Dřevínek, Pavel , Polineni, Deepika , Moskowitz, Samuel M , Ramsey, Bonnie W , Tullis, Elizabeth , Tian, Simon , Marigowda, Gautham , Nair, Nitin , McKee, Charlotte M , Mall, Marcus A , Taylor-Cousar, Jennifer L , Simard, Christopher , Waltz, David , Xuan, Fengjuan , Rowe, Steven M , Savage, Jessica , Vermeulen, François , Jain, Raksha , McKone, Edward F , Middleton, Peter G

in Adolescent / Adult / Aminophenols - administration & dosage / Aminophenols - adverse effects / Benzodioxoles - administration & dosage / Benzodioxoles - adverse effects / Child / Chloride Channel Agonists - administration & dosage / Chloride Channel Agonists - adverse effects / Chlorides - analysis / Clinical outcomes / Clinical trials / Collaboration / Conductance / Cystic fibrosis / Cystic Fibrosis - drug therapy / Cystic Fibrosis - genetics / Cystic Fibrosis - physiopathology / Cystic Fibrosis Transmembrane Conductance Regulator - genetics / Double-Blind Method / Drug Combinations / Female / Forced Expiratory Volume / Genotype / Genotypes / Humans / Indoles - administration & dosage / Indoles - adverse effects / Male / Mutation / Patients / Pharmaceuticals / Proteins / Pyrazoles - administration & dosage / Pyrazoles - adverse effects / Pyridines - administration & dosage / Pyridines - adverse effects / Pyrrolidines - administration & dosage / Pyrrolidines - adverse effects / Quality of life / Quinolones - administration & dosage / Quinolones - adverse effects / Statistical analysis / Stock options / Sweat - chemistry / Young Adult

2019

Yes Please

Hey, we have placed the reservation for you!

By the way, why not check out events that you can attend while you pick your title.

Oops! Something went wrong.

Looks like we were not able to place the reservation. Kindly try again later.

Are you sure you want to remove the book from the shelf?

Elexacaftor–Tezacaftor–Ivacaftor for Cystic Fibrosis with a Single Phe508del Allele

2019

Confirm

Do you wish to request the book?

Elexacaftor–Tezacaftor–Ivacaftor for Cystic Fibrosis with a Single Phe508del Allele

2019

Please be aware that the book you have requested cannot be checked out. If you would like to checkout this book, you can reserve another copy

How would you like to get it?

Submit

We have requested the book for you!

Your request is successful and it will be processed during the Library working hours. Please check the status of your request in My Requests.

Oops! Something went wrong.

Looks like we were not able to place your request. Kindly try again later.

Journal Article

Elexacaftor–Tezacaftor–Ivacaftor for Cystic Fibrosis with a Single Phe508del Allele

Lands, Larry C,

Dřevínek, Pavel,

Polineni, Deepika,

Moskowitz, Samuel M,

Ramsey, Bonnie W,

Tullis, Elizabeth,

Tian, Simon,

Marigowda, Gautham,

Nair, Nitin,

McKee, Charlotte M,

Mall, Marcus A,

Taylor-Cousar, Jennifer L,

Simard, Christopher,

Waltz, David,

Xuan, Fengjuan,

Rowe, Steven M,

Savage, Jessica,

Vermeulen, François,

Jain, Raksha,

McKone, Edward F,

Middleton, Peter G

2019

Overview

Triple treatment with elexacaftor, tezacaftor, and ivacaftor in patients with cystic fibrosis who had one Phe508del allele and a minimal-function mutation resulted in sustained improvement in FEV 1 , sweat chloride concentration, and the number of pulmonary exacerbations.

Share this book

Add to My Shelf

Publisher

Massachusetts Medical Society

Subject

Adolescent

/ Adult

/ Aminophenols - administration & dosage

/ Aminophenols - adverse effects

/ Benzodioxoles - administration & dosage

/ Benzodioxoles - adverse effects

/ Child