Catalogue Search | MBRL
Are you sure you want to remove the book from the shelf?
{{itemTitle}}
1
result(s) for
"Bodie, Susan"
Sort by:
Safety and Efficacy of Mitapivat in Pyruvate Kinase Deficiency
In this study, approximately half the patients with red-cell pyruvate kinase deficiency who were treated with mitapivat had an improvement in their hemoglobin level and decreased hemolysis that was sustained for nearly 3 years. Patients who had missense mutations that allowed for synthesis of a hypofunctioning enzyme were most likely to have a response.
Journal Article